| CO71 Investigating the Secondary Care System Burden of Glycogen Storage Disease Type IA (GSDIA) Using the HES Database |
| Author(s): E Kruger
S Chavda
RN Gupta
V Valayannopoulos |
| Affiliations(s): Ultragenyx Pharmaceutical Inc., Novato, CA, USA
IQVIA, London, UK
Ultragenyx Pharmaceutical Inc., Cambridge, MA, USA
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Publication(s): Kruger, E et al.
Value in Health, Volume 25, Issue 7, S317
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| Document Type(s): Abstract, Article, |
| Countries: England, |
| Click here for the abstract |
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Metabolic Disorders , Rare disease, Rare Diseases,
2022 |
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English
Burden of illness, clinical setting: Secondary care, Quality of life, |
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| Demographic characteristics, thromboembolism risk, and treatment patterns for patients with cold agglutinin disease in Japan |
| Author(s): Toyomi Kamesaki 1, Jun-Ichi Nishimura 2, Hideho Wada 3, Eric Yu 4, Elisa Tsao 5, Jaime Morales 5, Yuzuru Kanakura 2 6 (rwesheorj 4) |
| Affiliations(s): 1) Division of Support in Community Medicine, Center for Community Medicine, Regional Medical Center, Center for Regional Medical Care, Jichi Medical University, 3311 - 1 Yakushiji Shimotsuke-shi, Tochigi, Japan
2) Osaka University, Osaka, Japan
3) Kawasaki Medical School, Kurashiki, Japan
4) IQVIA Solutions K.K., Tokyo, Japan
5) Sanofi, Waltham, MA, USA
6) Sumitomo Hospital, Osaka, Japan |
Publication(s): International Journal of Hematology
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| Document Type(s): Article, |
| Countries: Japan, |
| Click here for the abstract |
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Rare Diseases,
2020 |
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English
Retrospective database analysis, |
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| Evidence synthesis in pulmonary arterial hypertension: a systematic review and critical appraisal |
| Author(s): Max Schlueter, Amélie Beaudet, Evan Davies, Binu Gurung, Andreas Karabis |
| Affiliations(s): IQVIA, 210 Pentonville Road, London, N1 9JY; IQVIA, Herikerbergweg 314, 1101 CT, Amsterdam, Netherlands; Department of Statistical Science, University College London, London, WC1E 6BT, UK. |
Publication(s):
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| Document Type(s): Article, |
| Countries: |
| Click here for the abstract |
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Comparative Effectiveness & Health Technology Assessment, Methodology, Rare Diseases,
2020 |
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A: |
English
Literature Review, Review, |
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| A network meta analysis comparing C1 and kallikrein inhibitors approved for prophylaxis of hereditary angioedema in the United States |
| Author(s): P. Saharia1, P. Soni2, M. Chatterjee3 |
| Affiliations(s): IQVIA, Gurugram, HR, India;
IQVIA, Delhi, India;
IQVIA, Gurugram, India |
Publication(s): DOI: https://doi.org/10.1016/j.jval.2019.04.1641
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| Document Type(s): Article, |
| Countries: USA, |
| Click here for the abstract |
C:
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Cardiovascular disease, Rare Diseases,
2019 |
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L:
A: |
English
Literature Review, Meta analysis, |
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| Identification of a hereditary angioedema cohort in a US ambulatory EMR database |
| Author(s): Brouwer E, Bratton E, Near A, Lang K, Mack C |
| Affiliations(s): |
Publication(s): Pharmacoepidemiol Drug Saf 2018; 27 (2): 136-137.
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| Document Type(s): Poster, |
| Countries: |
C:
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Rare Diseases,
2018 |
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English
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| Rare disease development programs: An update |
| Author(s): Wu J, Want C, Horton DB, Petersen I, Oliveria S, Blackburn S, Jiang J, LoCasale R. |
| Affiliations(s): |
Publication(s): Pharmacoepidemiol Drug Saf 2018; 27 (2):5.
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| Document Type(s): Poster, |
| Countries: |
C:
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Rare Diseases,
2018 |
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L:
A: |
English
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| WHAT INTERPRETATION OF ICERS IN ORPHAN DISEASES? A FRENCH EXAMPLE. |
| Author(s): Moutier Hélène; Bourguignon Sandrine; Maurel Frédérique; Bodaghi Charles |
| Affiliations(s): RWI IQVIA France |
Publication(s): ISPOR 2018
|
| Document Type(s): Poster, |
| Countries: France, |
C:
Y: |
Comparative Effectiveness & Health Technology Assessment, Health economics, Pricing and reimbursement, Rare Diseases,
2018 |
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A: |
English
Cost effectiveness, Pricing & Reimbursement, Willingness to pay, |
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| Healthcare resource utilization and costs associated with long-term corticosteroid exposure in patients with systemic lupus erythematosus |
| Author(s): Kabadi S, Yeaw J, Bacani AK, Tafesse E, Bos K, Karkare S, DeKoven M, Vina ER |
| Affiliations(s): AstraZeneca, IQVIA |
Publication(s): Lupus
|
| Document Type(s): Article, |
| Countries: USA, |
| Click here for the abstract |
C:
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Rare Diseases,
2018 |
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L:
A: |
English
Cost analysis, Retrospective cohort analysis, |
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| Health Care Resource Utilization Among a US Cohort Treated for Hereditary Angioedema, 2010–2015 |
| Author(s): Tachdjian R, Johnson KE, Casso D, Oliveria SA, Devercelli G, Jain G. |
| Affiliations(s): Tachdjian R: UCLA School of Medicine; Johnson KE: IQVIA (formerly); Casso D: IQVIA; Oliveria SA: IQVIA; Devercelli G: Shire; Jain G: Shire |
Publication(s): 2018 American Academy of Allergy, Asthma and Immunology (AAAAI)/World Allergy Organization (WAO) Joint Congress
|
| Document Type(s): Poster, |
| Countries: USA, |
C:
Y: |
Patient Registries & Real-World Study Methods, Rare Diseases,
2018 |
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L:
A: |
English
Cost analysis, Database Study, Epidemiological study, Retrospective database analysis, |
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| Demographic Characteristics and Treatment Patterns among Patients Treated for Hereditary Angioedema in a U.S. Cohort, 2006-2015 |
| Author(s): Tachdjian R, Johnson KE, Casso D, Oliveria SA, Devercelli G, Jain G |
| Affiliations(s): Tachdjian R: UCLA School of Medicine (Department of Medicine and Pediatrics), Johnson KE: IQVIA (formerly); Casso D: IQVIA; Oliveria SA: IQVIA; Devercelli G: Shire; Jain G: Shire. |
Publication(s): 34th International Conference on Pharmacoepidemiology & Therapeutic Risk Management
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| Document Type(s): Abstract, |
| Countries: USA, |
C:
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Rare Diseases,
2018 |
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L:
A: |
English
Database Study, Epidemiological study, Retrospective cohort analysis, Retrospective database analysis, |
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